Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for ...

Ann Blake, from Godshill, suffers from muscular dystrophy and released a book in 2024 titled 'A Legacy of Love' to share ...

Johnny Quintana’s life changed at the age of 19 when he was diagnosed with a rare form of muscular dystrophy called ...

Police are searching for a suspect after a brief standoff involving SWAT on the north side of Indianapolis Tuesday night. A ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...

The Muscular Dystrophy Association (MDA) proudly announces the launch of its 75th anniversary campaign, marking a legacy of progress in research, care, ...

The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...

Teen Mom star Leah Messer admits it’s “very challenging” helping daughter Aliannah “balance” her desire for freedom with the ...

(IN BRIEF) Roche has reported positive results from the second year of the EMBARK Phase III trial of Elevidys (delandistrogene moxeparvovec), the first approved gene therapy for Duchenne muscular ...

The data showed reduced difficulties in standing, walking and running that were statistically significant, the company said.

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...