In trials at University College London Hospitals (UCLH), an ASO is being used to target the mutated gene that results in the ...
Roche has reported positive results from the second year of the EMBARK Phase III trial of Elevidys (delandistrogene moxeparvovec), the first approv ...
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5 US Longevity and Anti-aging Stocks to Watch in 2025As the percentage of the global population over 65 continues to increase, the popularity of anti-aging stocks is rising in ...
MeiraGTx's financials show $125 million in cash, but additional funding will be needed within the next 12 months. Click for ...
Explore the role of preclinical MRI in studying neurological diseases, with a focus on advanced cellular and molecular ...
AskBio Inc. (AskBio), a gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, announced that the first participants have been randomized in its phase II clinical ...
The STEER study confirmed the therapy's favorable safety profile, with adverse events similar to the control group. OAV101 IT is a one-time gene therapy designed to replace the function of the ...
Newly discovered Parkinson’s disease gene among East Asians enhances potential for early detection
Approaches towards the discovery of rare SMPD1 variants that increase Parkinson’s disease risk in East Asians. Image credit: Elaine Chew The SMPD1 gene encodes instructions for making acid ...
The company is advancing its Phase I/II trial and exploring accelerated approval pathways in the US and Europe.
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