Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for ...

Listen to this article The Virginia Home plans to build a $128 million, 75-acre campus in Hanover County, according to a Thursday announcement by the nonprofit, which serves adults with irreversible ...

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.

Tony, from Skellingthorpe, Lincoln, was diagnosed with myofibrillar myositis and anti-SRP immune-mediated necrotizing ...

Columnist Betty Vertin has learned that as a parent, she's finding the years with all her children, including those with DMD, too short.

Nonprofits that challenged to the Trump administration’s freezing of grant funds highlighted crisis for a small center in ...

Scientists at the University of Exeter have identified an unexpected potential contributor to human health and longevity: ...

Shares of PTC Therapeutics, Inc. (NASDAQ:PTCT – Get Free Report) shot up 6.1% during trading on Monday after Cantor Fitzgerald raised their price target on the stock from $76.00 to $113.00. Cantor ...

It was the type of upsetting yet commonplace problem most parents face from time to time. Early last month, the Taylor family were on their way home from a meal out when Trey, 11, began feeling sick.

Patty Metzler has been at Carle for so long that when she started there were four hospitals in Champaign-Urbana.

A renewed focus on the potentially transformative effect of cell and gene therapies (CGTs) will help businesses developing such treatments to attract investment and persuade policymakers to affect ...