A new UCLA Health study has discovered in mouse models that genes associated with repairing mismatched DNA are critical in ...

Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...

It suggests the treatment approach tried with mixed success in recent years isn't the only way to disrupt the disease ‒ and it lays a clear path for what may be a better one. Huntington's ...

Less than a month after researchers unveiled that a “ticking DNA clock” is behind Huntington’s disease (HD), scientists have ...

New results from an ongoing phase 1/2 study of the therapy showed that it was able to slow down disease progression in patients with early-stage Huntington's over two years compared to an ...

The findings suggest that there is a treatment window, potentially decades before symptoms are present, where those at risk of developing Huntington’s disease are functioning normally despite ...

Shares in gene therapy developer uniQure have risen more than 75% after the company reported that Huntington’s disease candidate AMT-130 slowed down the progression of the disorder over two years.

Huntington's disease is a neurodegenerative disorder that is usually fatal about 15 to 20 years after a patient is diagnosed. It is known ... | Genetics And Genomics ...

The findings suggest that there is a treatment window, potentially decades before symptoms are present, where those at risk of developing Huntington's disease are functioning normally despite ...

Using CRISPR technology, scientists uncovered genes that control C-A-G genetic stumbles in Huntington's disease ...

The findings suggest that there is a treatment window, potentially decades before symptoms are present, where those at risk of developing Huntington's disease are functioning normally despite ...

The findings suggest that there is a treatment window, potentially decades before symptoms are present, where those at risk of developing Huntington's disease are functioning normally despite ...