Could viral infections play a role in Huntington's disease? Research suggests Apolipoprotein B mRNA editing catalytic ...

Boosting communication between the spinal nerves and the muscles using the spinal cord stimulation reverses spinal muscle atrophy (SMA) progression and could be applied to other motoneuron diseases, ...

H.C. Wainwright analyst Patrick Trucchio has reiterated their bullish stance on QURE stock, giving a Buy rating on January 21.Invest with ...

New genetic research shows why some people develop deadly Huntington's disease earlier than others. The findings could lead to better treatments.

LEXINGTON, Mass. - uniQure N.V. (NASDAQ: NASDAQ:QURE), a gene therapy company with a market capitalization of $767 million, ...

A new drug-free, minimally invasive intervention targets the root cause of progressive loss of neural function in spinal muscle atrophy (SMA), an inherited neuromuscular disease.

PTC Therapeutics, Inc. (NASDAQ:PTCT), a biopharmaceutical company focused on developing and commercializing novel medicines for rare disorders, finds itself at a critical juncture. With a promising ...

A research team has discovered intricate molecular mechanisms driving the RNA processing defects that lead to Huntington's disease and ... additional avenues for treatment. While it's known ...

A new window of opportunity for therapy Robert Handsaker is a staff ... More than 2,000 Australians are believed to have Huntington's disease — an inherited disorder. When a parent has the ...

Huntington's disease kills a population of cells called ... He adds that slowing down certain DNA-maintenance processes with a molecular therapy might slow down DNA-repeat expansion by allowing ...