News Medical on MSN17h
Gene therapy breakthrough offers hope for severe Dravet syndrome cases
AAV-Navβ1 gene therapy effectively reduces seizures and prolongs life in a mouse model of SCN1B-linked Dravet syndrome, ...
Solid Biosciences Reports Positive Initial Clinical Data from Next-Generation Duchenne Gene Therapy Candidate SGT-003
Day 90 biopsy data reported from first 3 participants dosed in Phase 1/2 INSPIRE DUCHENNE trial —— Average microdystrophin expression of 110% ...
BioPharma Dive10h
Biogen buys rights to Stoke’s rare epilepsy drug
In exchange for $165 million, Biogen now has access to zorevunersen, a potential first-of-its-kind treatment for Dravet ...
Solid Biosciences Announces Pricing of Underwritten Offering
This press release shall not constitute an offer to sell, or a solicitation of an offer to buy these securities, nor shall there be any sale of, these securities in any state or jurisdiction in which ...
Equus Magazine7h
3 Utah Horses Test Positive for EHV-1
Three horses in Utah recently tested positive for equine herpesvirus-1 (EHV-1). Two horses live in Duchesne County and are under official quarantine. One horse lives in Box Elder County; this horse ...