Spring Fashion Week is officially underway, and walking in one of the shows is everyone’s favorite TV scientist, Bill Nye.

Cure Rare Disease (CRD) announced it has been awarded a $5.69 million grant from the California Institute for Regenerative ...

Spinocerebellar ataxia type 3 (SCA3 ... SCA3 results from a mutation that causes a toxic accumulation of trinucleotide repeats. Cure Rare Disease (CRD) is a nonprofit biotechnology company ...

At this time, I'd like to welcome everyone to the Biogen fourth-quarter and full-year 2024 earnings call and business update. (Operator Instructions) Today's conference is being recorded. Thank you. I ...

Q4 2024 Earnings Conference Call February 12, 2025 8:30 AM ETCompany ParticipantsTim Power - Head of IRChris Viehbacher ...

FA is known to cause progressive nervous system damage ... including Duchenne muscular dystrophy (Duchenne), Friedreich’s ataxia (FA), catecholaminergic polymorphic ventricular tachycardia (CPVT), ...

Quince Therapeutics, Inc. (Nasdaq: QNCX) is a late-stage biotechnology company dedicated to unlocking the power of a patient's own biology for the treatment of rare diseases. For more information on ...

Friedreich's Ataxia [FA] is a type of disorder characterized ... factor of which would be the targeting of the underlying cause of FA and all manifestations of the disease that might occur.

Larimar’s lead compound, nomlabofusp, is being developed as a potential treatment for Friedreich's ataxia. Larimar also plans to use ... uncertainties and other factors that may cause actual results, ...