Novartis is seeking to repurpose its investigational oral spinal muscular atrophy (SMA) drug branaplam to treat Huntington's disease, the Swiss drugmaker said on Wednesday, as it plans a clinical ...
Spinal muscular atrophy affects all the body's muscles. For a long time, it was considered a disease caused solely by the ...
Spinal muscular atrophy (SMA) is a severe neurological disease for which there is presently no cure, although current therapies can alleviate symptoms. In the search for better treatment options, ...
In a closely watched case, Roche suffered a setback as a court said it would permit a generic version of its rare disease ...
As their 8-month-old daughter prepares for gene therapy treatment, a Coon Rapids family is bracing for three months of ...
Affordable Risdiplam is now within reach for Spinal Muscular Atrophy (SMA) patients in India, thanks to a Delhi High Court ...
According to the National Institute of Neurological Disorders and Stroke, there are currently only three FDA-approved ...
The Delhi High Court has dismissed Roche's appeal, allowing Natco to launch a generic version of Risdiplam for spinal ...
The FDA in September issued two rejections for spinal muscular atrophy therapies—both linked to manufacturing problems—and ...
Spinal muscular atrophy (SMA) is a severe neurological disease for which there is presently no cure, although current therapies can alleviate symptoms. In the search for better treatment options, ...