Paroxysmal nocturnal hemoglobinuria (PNH) is a rare, acquired, life-threatening disease of the blood. The disease is characterized by destruction of red blood cells, blood clots, and impaired bone ...

A novel drug combination, improvements in quality of life, and breakthrough hemolysis control are among the clinical highlights in paroxysmal nocturnal hemoglobinuria (PNH) presented at the 2024 ...

The mainstay of therapy for the rare blood disease paroxysmal nocturnal hemoglobinuria (PNH) is Alexion's infusion therapy Soliris, but Novartis' iptacopan could provide an oral option after ...

1-5 All of these symptoms, mild or severe, could be a sign of a rare, chronic, and serious blood disorder called paroxysmal nocturnal hemoglobinuria (PNH), one of a number of diseases that involve the ...

Contact the study team to discuss study eligibility and potential participation. Patients of any age, including minors, with a diagnosis of PNH or a detected PNH clone, including patients previously ...