An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Having found that in biomedical research, the Bird Rock resident and scientist at La Jolla’s Sanford Burnham Prebys has ...

Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, ...

Secure loose outdoor objects. && EAST STROUDSBURG, Pa. - She's a student on a mission, trying to help people with muscular dystrophy one shamrock at a time. East Stroudsburg University's Alexa ...

Researchers focused on Myotonic Dystrophy 1 heart problems are testing a novel approach to restore normal function.

A Portland nonprofit is rewriting the story for people with disabilities by offering jobs, mentorship, and scholarships, ...

U.S. Sen. Richard Blumenthal and researchers raise the alarm on how a federal medical research funding cap could impact "life ...

New Evrysdi five-year data from the SUNFISH study showed continued stabilisation of motor function in a broad population of ...

Angus Drummond, founder of disabled-friendly travel specialist Limitless Travel, has urged the industry to stop making ...

While plenty of people are going green in honor of Saint Patrick's Day, one student at East Stroudsburg University is turning ...